Orphazyme A/S AAQS 2024

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Orphazyme A/S is a Danish biopharmaceutical company specializing in the development of therapies for rare neurodegenerative diseases. They focus on researching amyloids, insoluble protein complexes found in various neurodegenerative diseases. Their business model involves developing and marketing therapeutic treatments for these rare neurodegenerative diseases. They specialize in four disease areas: Niemann-Pick disease type C (NPC), Gaucher disease, sporadic inclusion body myositis (sIBM), and amyotrophic lateral sclerosis (ALS). They concentrate on developing drugs that control lysosomal function and the breakdown of biocatalysts. Their advanced product, Arimoclomol, is currently being tested in a Phase 3 trial for the treatment of NPC disease. Orphazyme has collaborations with other companies and research institutions to advance their research and development efforts. These include a partnership with Sobi for the exclusive rights to market Arimoclomol in Europe and a collaboration with QIAGEN to develop biomarkers for diagnosing NPC disease. Overall, Orphazyme is a promising company focused on providing much-needed solutions for rare neurodegenerative diseases through their pipeline of therapies. They are well-positioned to become a leading player in the biopharmaceutical industry in the future. Orphazyme A/S ist eines der beliebtesten Unternehmen auf Eulerpool.com.