Gensight Biologics AAQS 2025

What does Gensight Biologics do?

Gensight Biologics SA is a biotechnology company specializing in the development of gene therapies for genetically inherited eye diseases. The company is based in Paris, France, with offices in Amsterdam and New York. The company's history began in 2012 when the founder, Bernard Gilly, had the idea to develop gene therapy for liver diseases. After several years of research and development, it became clear that the company could not develop a commercially viable solution due to the complexity of liver diseases and the high treatment costs. In 2013, the company shifted its focus to the development of gene therapies for genetically inherited eye diseases. Since then, Gensight Biologics SA has conducted several studies and clinical trials and is now a leading provider in this market segment. Gensight Biologics SA's business model is based on the development of gene therapies aimed at correcting the genetic defect and repairing the corresponding cells in the eye. The gene therapy is conducted using adeno-associated viruses (AAV), which introduce a normal gene into the diseased tissue. Gensight Biologics' particular focus is on the development of gene therapies for the treatment of eye diseases, with a focus on the research and treatment of rare diseases. The company has two central product lines. Firstly, it offers gene therapies targeting genetically inherited eye diseases such as retinitis pigmentosa (RP). This disease is inherited and leads to gradual loss of vision and, in severe cases, blindness. Gene therapy aims to repair the responsible gene and improve cell function and vision. Secondly, Gensight Biologics SA offers gene therapies targeting liver diseases such as Wilson's disease and gout, where copper and uric acid, respectively, are not properly metabolized. Here, gene therapy aims to repair the corresponding gene and reduce disease-related functional impairments. Gensight Biologics SA works closely with regulatory authorities and clinical partners to ensure the safety and efficacy of their gene therapies. The therapies are currently being tested in clinical trials to assess their effectiveness and safety. Gensight Biologics SA also collaborates with some of the world's leading doctors and researchers in the field of ophthalmology. While Gensight Biologics SA's gene therapies are still in the development phase, the clinical trials have shown promising results, and the company expects their therapies to be approved soon. The company follows a well-thought-out growth model and plans to develop further products for the treatment of eye diseases in the future. Overall, Gensight Biologics SA is a biotechnology company specialized in gene therapies, with a focus on researching and treating rare eye diseases. The company presents a promising investment option due to its innovative product range, close collaboration with researchers and clinical partners, and solid growth strategy. Gensight Biologics ist eines der beliebtesten Unternehmen auf Eulerpool.com.