Alexion Pharmaceuticals Inc is a global biopharmaceutical company that focuses on rare diseases. The company specializes in developing therapies for patients with rare genetic disorders and other serious illnesses that affect the immune system. Alexion pursues a forward-thinking business model aimed at innovation and expansion strategies to further build and diversify its portfolio.
The main business areas of Alexion Pharmaceuticals include:
1. Orphan Diseases - Alexion focuses on disorders that affect fewer than 200,000 patients in the United States, utilizing their deep understanding of the human protein system to develop new therapies and save lives. The company currently has various successful products for rare diseases in its portfolio, including the C5 complement inhibitor Soliris, the drug Ultomiris, and the polyethylene glycol hemophilia B product Strensiq.
2. Neurology - In December 2019, Alexion Pharmaceuticals announced its intention to expand its portfolio to include neurological disorders. The company currently has early and late-phase clinical trials for various novel treatment methods, including therapies for myasthenia gravis, neuromuscular disorders, and cerebral infarction.
3. Oncology - Although Alexion products are not directly effective in the field of oncology, the company has developed a platform for the discovery of targeted antibodies against medically significant targets. Alexion is currently collaborating with leading biotech companies and academic institutions to make further groundbreaking discoveries.
The company has several innovative products in the clinical stage with excellent chances of success. Soliris, Alexion's first approved C5 complement inhibitor, is currently approved in over 55 countries. This therapy is used in patients with paroxysmal nocturnal hemoglobinuria, atypical hemolytic-uremic syndrome, and hemolytic anemia. The drug is also currently being studied in clinical trials for patients with neuromuscular disorders, and it has recently been used against Covid-19.
Ultomiris, the next generation of Soliris, is a long-acting C5 inhibitor that is subcutaneously injected every 8 weeks, unlike Soliris, which requires weekly administration. The drug has shown efficacy in patients who were already on Soliris therapy. Ultomiris is currently approved for the treatment of paroxysmal nocturnal hemoglobinuria and atypical hemolytic-uremic syndrome.
Strensiq, a recombinant enzyme, was specifically developed for patients with rare bone diseases such as hypophosphatasia. It enables.
Alexion Pharmaceuticals pursues a strategy of financial stability and profitable development. The company aims to achieve technological superiority through smart investments in research and development, expand into new therapeutic patient populations, and seek geographic expansion and diversification. Through its intensive research activities, Alexion Pharmaceuticals continues to develop innovative and groundbreaking products to improve the lives of patients with rare and serious diseases.
Translation:
Alexion Pharmaceuticals Inc is a global biopharmaceutical company specializing in rare diseases. It develops therapies for patients with rare genetic disorders and other serious immune system illnesses. With a focus on innovation and expansion, the company aims to build and diversify its portfolio. Alexion's main business areas are orphan diseases, neurology, and oncology. It has successful products for rare diseases, such as Soliris, Ultomiris, and Strensiq. Alexion is also involved in clinical trials for innovative treatments in neurology. Although it doesn't directly impact oncology, it collaborates with biotech companies and academic institutions for targeted antibody discoveries. Financial stability and profitable development are prioritized, with investments in research and development and geographic expansion. Through its research efforts, Alexion strives to improve the lives of patients with rare and serious diseases.
